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  • Organizations: VeonGen Therapeutics
FDA grants RMAT designation to VeonGen's Stargardt therapy
Pipeline

FDA grants RMAT designation to VeonGen's Stargardt therapy

Status marks third designation for the VG801, intended to treat patients with biallelic
ViGeneron rebrands as VeonGen Therapeutics with new FDA designation
Pipeline

ViGeneron rebrands as VeonGen Therapeutics with new FDA designation

German-based genetic medicine company also receives a Rare Pediatric Disease Designation for its Stargardt disease gene therapy candidate.
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