Category

• Pipeline1
• Research1

Organizations

• Bausch + Lomb64
• Eyes On Eyecare42
• Alcon, Inc.41
• American Optometric Association34
• Harrow26
• Glaukos25
• Regeneron21
• Aldeyra Therapeutics20
• Sight Sciences19
• American Academy Of Ophthalmology18

Tags

• Gene Therapy2
• Retina2
• FDA1
• Stargardt Disease1
• Clinical Trials1
• Inherited Retinal Disease1
• Partnership1

• Organizations: SpliceBio✕

Clear all

Pipeline

FDA clears SpliceBio's IND of gene therapy for Stargardt trial

Clearance represents a significant milestone as the first-ever IND for a protein-splicing gene therapy designed to target the genetic root cause of this disease.

Research

SpliceBio and Spark Therapeutics partner on IRD gene therapy

Collaboration will look to incorporate SpliceBio’s proprietary platform for protein splicing.